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Complex Chronic Conditions and Rare Diseases
Complex Chronic Conditions and Rare Diseases

With millions of individuals affected by these conditions, there is a critical need for innovative treatments and solutions. Unfortunately, due to regulatory and financial barriers, only a small percentage of patients can benefit from available therapies.

At Genaxya, we strive to bring vital treatments to patients through extensive collaboration with global providers and healthcare partners. Our carefully selected product portfolio covers important therapeutic domains that address areas of high unmet medical needs.

With a deep commitment to patient-centric care, we will build on our portfolio to improve access to life-saving therapies and enhance the quality of life for those facing these challenging medical conditions.

Discover how our innovative pharmaceuticals are making a difference in the lives of those facing unique health challenges.
Gaucher syndrome
Huntington's disease
Pulmonary arterial hypertension (PAH)
Acute lymphocytic leukemia (ALL)
B-cell chronic lymphocytic leukemia (CLL)
Hodgkin's disease
Paroxysmal nocturnal hemoglobinuria (PNH)
Dravet syndrome
Advanced renal cell carcinoma
Hepatocellular carcinoma
Breast cancer
Advanced ovarian carcinoma
Metastatic ovarian carcinoma
Small cell lung carcinoma
Ewing sarcoma
Hereditary angioedema (HAE)
Multiple sclerosis